Genetic Diseases, Inborn
Also known as: Genetic Disease, Inborn / Inborn Genetic Diseases
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00741 | Hydrocortisone | 1 | Completed | 1 |
| DB18620 | AOC 1001 | 2 | Active Not Recruiting | 1 |
| DB15744 | Allogeneic Cardiosphere-Derived Cells | 2 | Completed | 1 |
| DB12023 | Benralizumab | 2 | Completed | 1 |
| DB05528 | Mipomersen | 2 | Completed | 2 |
| DB15572 | Exagamglogene autotemcel | 2 / 3 | Active Not Recruiting | 1 |
| DB14973 | Abrocitinib | 3 | Completed | 2 |
| DB15744 | Allogeneic Cardiosphere-Derived Cells | 3 | Recruiting | 1 |
| DB05016 | Ataluren | 3 | Completed | 2 |
| DB05016 | Ataluren | 3 | Terminated | 1 |
| DB12159 | Dupilumab | 3 | Completed | 1 |
| DB15572 | Exagamglogene autotemcel | 3 | Enrolling by Invitation | 1 |
| DB15572 | Exagamglogene autotemcel | 3 | Recruiting | 2 |
| DB05528 | Mipomersen | 3 | Completed | 2 |
| DB14890 | Obicetrapib | 3 | Active Not Recruiting | 1 |
| DB06372 | Rilonacept | 3 | Completed | 1 |
| DB01018 | Guanfacine | 4 | Recruiting | 1 |
| DB01076 | Atorvastatin | Not Available | Completed | 1 |
| DB01039 | Fenofibrate | Not Available | Completed | 1 |
| DB00627 | Niacin | Not Available | Completed | 1 |